Publications & Posters
Scholarly publications
Spinal Muscular Atrophy
Apitegromab
March 2026
Muscular Dystrophy Association Clinical & Scientific Conference 2026
Meaningfulness of ‘any point change’ or ‘stabilization’ in the HFMSE on the psychosocial well-being of adult patients with spinal muscular atrophy
Spinal Muscular Atrophy
Apitegromab
March 2026
Muscular Dystrophy Association Clinical & Scientific Conference 2026
Post hoc analyses from the Phase 3 SAPPHIRE study evaluating apitegromab in patients with nonambulatory type 2 or 3 spinal muscular atrophy
Spinal Muscular Atrophy
Apitegromab
February 2026
Expert Review of Neurotherapeutics
Advancing treatment of spinal muscular atrophy through inhibition of the myostatin signaling pathway
Spinal Muscular Atrophy
Apitegromab
February 2026
Treat-NMD International Conference
Understanding adult patient perspectives on the clinical meaningfulness of “any point differences” on the Hammersmith Functional Motor Scale–Expanded in SMA
Spinal Muscular Atrophy
Apitegromab
February 2026
Treat-NMD International Conference
Assessing the impact of “any point differences” or “stability” in the Hammersmith Functional Motor Scale–Expanded on activities of daily living in adult patients with SMA
Immuno-Oncology
Linavonkibart
January 2026
Linavonkibart publication