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Scholar Rock

Discovery and Development of Innovative Medicines

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    Discover how our breakthrough approach treats complex disease at its biological root.

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HomePatients & FamiliesAreas of Focus

Areas of Focus

Muscling out the root of disease

Scholar Rock focuses on discovering and developing breakthroughs in medical conditions where proteins called growth factors play a role in the biology of the disease. Our untraditional approach of targeting latent, or upstream, protein growth factors is helping us to succeed where other approaches may have failed. Read below for how we apply this approach.

Spinal Muscular Atrophy

Scholar Rock is at the forefront of muscle-targeted breakthroughs to transform the treatment of rare neuromuscular diseases like spinal muscular atrophy.

Learn more about our focus on SMA

Learn more about our medicines

Accelerate Breakthroughs

There is no time to waste. We are determined to discover, develop, and deliver new possibilities for patients.

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Scholar Rock, Inc.
301 Binney Street, 3rd Floor
Cambridge, MA 02142

Phone: 857.259.3860
[email protected]

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We are Scholar Rock.

A biopharmaceutical company dedicated to discovering, developing, and delivering therapies that create new possibilities for patients.

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