We create new possibilities through cutting-edge science.
At Scholar Rock, we are on a mission to discover, develop, and deliver therapies to improve people’s lives.
We are a biopharmaceutical company combining bold science with a deep commitment to make a meaningful difference for people living with serious diseases.
We take a unique approach to treating disease.
Our scientific approach allows us to selectively target a class of proteins in a unique way. These proteins—called growth factors—control a range of biological functions.
Our approach aims to selectively target protein growth factors before they are activated—like shutting off the water supply before a faucet starts leaking. Traditional approaches instead focus on “mopping up” the water after it has already spilled.
We push boundaries for patients in need.
We are applying this approach to diseases where protein growth factors play a central role. Learn more about our pipeline of investigational therapies in development here.
September 30, 2024
Caregiver perspectives on creating possibilities for loved ones living with SMA
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What do new possibilities mean to those living with SMA?
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