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Scholar Rock

Scholar Rock

Discovery and Development of Innovative Medicines

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      • Spinal Muscular Atrophy
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    Learn about our commitment to creating possibilities for those living with serious disease.

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    Meet Scholar Rock, a biopharmaceutical company committed to improving lives.

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    Discover how our breakthrough approach treats complex disease at its biological root.

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    • Neuromuscular and Obesity
      • Spinal Muscular Atrophy
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HomePatients & FamiliesAreas of Focus

Areas of Focus

Muscling out the root of disease

Scholar Rock focuses on discovering and developing breakthroughs in medical conditions where proteins called growth factors play a role in the biology of the disease. Our untraditional approach of targeting latent, or upstream, protein growth factors is helping us to succeed where other approaches may have failed. Read below for how we apply this approach.

Spinal Muscular Atrophy

Scholar Rock is the first company to show clinical proof of concept for a muscle-targeted treatment in spinal muscular atrophy (SMA). Apitegromab is an investigational therapy that has the potential to transform the standard of care for people living with SMA.

Learn more about our focus on SMA

Accelerate Breakthroughs

There is no time to waste. We are determined to discover, develop, and deliver new possibilities for patients.

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Scholar Rock, Inc.
301 Binney Street, 3rd Floor
Cambridge, MA 02142

Phone: 857.259.3860
[email protected]

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We are Scholar Rock.

A biopharmaceutical company dedicated to discovering, developing, and delivering therapies that create new possibilities for patients.

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    • Neuromuscular and Obesity
      • Spinal Muscular Atrophy
      • Cardiometabolic Disorders
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      • Cancer (solid tumors)
    • Fibrotic Diseases
      • Fibrosis
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      • Anemia
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      • Archived Press Releases
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