We want to see things from your perspective. We seek to collaborate with other biotechs, pharmaceuticals, universities, and organizations who want to combat disease from a new angle.
“We have an extraordinary team committed to our science and our patients.”
Nagesh Mahanthappa, PhD, MBA
Interim CEO

Asset Development
Janssen Pharmaceuticals
Collaborating in Patient Advocacy
Spinal Muscular Atrophy

SMA Foundation

CureSMA

SMA Europe