Areas of Focus
Muscling out the root of disease
Scholar Rock focuses on discovering and developing breakthroughs in medical conditions where proteins called growth factors play a role in the biology of the disease. Our untraditional approach of targeting latent, or upstream, protein growth factors is helping us to succeed where other approaches may have failed. Read below for how we apply this approach.
Spinal Muscular Atrophy
Scholar Rock is the first company to show clinical proof of concept for a muscle-targeted treatment in spinal muscular atrophy (SMA). Apitegromab is an investigational therapy that has the potential to transform the standard of care for people living with SMA.
Accelerate Breakthroughs
There is no time to waste. We are determined to discover, develop, and deliver new possibilities for patients.
